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Thank you for visiting my JustGiving page. On Friday 24th June, I will be taking part in a 30km "Big Walk" in support of Genetic Disease Research at the University of Sheffield. Any donations are appreciated to help reach my fundraising goal!
The University of Sheffield is pioneering gene therapy treatments that could offer hope for patients living with severe and hard to treat genetic diseases. Although individually uncommon, collectively it's estimated that rare diseases may affect up to 10% of the world's population. In the UK alone, 1 in 25 babies are born with a genetic disorder. Sheffield’s research will change the lives of families who are desperately seeking a treatment for their loved-one.
Sheffield’s scientists have discovered a way to engineer bespoke genes to replace or silence a faulty one. In the form of a safe ‘viral vector’ these gene therapies will be manufactured in Sheffield and delivered to patients around the world.
Your support for this research really will save lives.