Charcot Marie Tooth disease is a rare genetic disease that causes damage to the peripheral nerves affecting hands and feet and often making walking and running challenging or impossible. CMT4C is a rare subtype of this already rare disease caused by inheriting two copies of the recessive gene. But despite CMT4C being incredibly rare, there is already a promising roadmap to a potential treatment.

We also have a specific CMT4C project underway called Project Foresee. Project Foresee is a CMTA-sponsored initiative focused on advancing the most promising gene therapy for CMT4C. Supported by world-leading scientists, this groundbreaking project aims to treat—and ultimately cure—the first handful of CMT4C patients within the next three years.

Please note that the Project Foresee JustGiving page is separate from this page. If you are interested in learning more about or supporting Project Foresee, please CLICK HERE.

We have identified exactly the right researchers to do this work, but now we need your help! The CMT4C community is small, so it is up to us, with the support of the CMTA and our communities to raise the funds to push forward with research for treatment options. Please help us foresee the end of 4C!

The CMT4C Advocacy Group is working to connect those affected by Charcot-Marie-Tooth disease type 4C: patients, loved ones and the organizations and researchers who are developing treatments. For more information, please visit the CMT4C Advocacy Group.